WHITEPAPER
GENE THERAPY
Gene therapy promises to hold the cure to a number of diseases which, until now, have been considered incurable. By replacing a faulty gene in a patient’s DNA or repairing a defective gene by gene editing, gene therapy can provide a one-time treatment option for diseases such as genetic blindness, muscular dystrophy, blood cancer. Read our recent whitepaper: Advancements in gene therapy – usage of AAV vectors here.
Download PDF